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Developing an mRNA Therapy for DMD with Elixirgen Therapeutics' Aki Ko

15 min • 6 juni 2024

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Elixirgen Therapeutics' Aki Ko joins Erin Harris to detail the company's Bobcat mRNA therapeutic and how it differs from traditional exon-skipping drugs and AAV-microdystrophin in treating DMD. Regarding delivery, Ko explains the advantage of the mRNA approach over the AAV approach.

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